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Maja Di Rocco

Chief Unit Rare Diseases, Department of Pediatrics · IRCCS Istituto Giannina Gaslini

https://researchid.co/diroccomaja
@gaslini.org
283Scopus Publications
13480Google Scholar Citations
63Google Scholar h-index
198Google Scholar i10-index

Research Interests

Genetic diseases, Metabolic diseases

Education

Main Degree:Medicine and Surgery, Universitiy of Genoa, 1979 Postgraduated degree Pediatrics,University of Genoa 1984 Postgraduated degree Pediatric Neurology and Psychiatry ,University of Genoa, 1987

Recent Scopus Publications

  1. Mitochondrial energetic failure underlies FLVCR1-related sensory neuropathy
    Communications Biology, 2026
  2. Hearing loss predictive model in fibrodysplasia ossificans progressiva from a national referral center: developing an hearing loss predictive model
    Jbmr Plus, 2025
  3. The European reference network for metabolic diseases (MetabERN) clinical pathway recommendations for Pompe disease (acid maltase deficiency, glycogen storage disease type II)
    Orphanet Journal of Rare Diseases, 2024
  4. Characterization of flare-ups and impact of garetosmab in adults with fibrodysplasia ossificans progressiva: A post hoc analysis of the randomized, double-blind, placebo-controlled LUMINA-1 trial
    Journal of Bone and Mineral Research, 2024
  5. Dysregulation of FLVCR1a-dependent mitochondrial calcium handling in neural progenitors causes congenital hydrocephalus
    Cell Reports Medicine, 2024

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